The treatment, the first of its kind, was approved by the Food and Drug Administration on Thursday. “Our baby was born deaf, and now he can hear,” said one parent.
Category: Genetic Engineering
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New Gene Therapy Enables Children With a Rare Form of Deafness to Hear
The New York Times – Business: -
How to Turn a Chicken Egg Into a Drug Factory
The New York Times – Business:A biotech start-up is testing a novel way of efficiently producing pharmaceutical drugs.
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F.D.A. Sharply Limits Use of Drug Linked to Two Teen Deaths
A gene therapy for Duchenne muscular dystrophy caused complications to the liver, prompting a review of its use for younger patients.
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William J. Rutter, Biotech Pioneer of Gene-Based Medicine, Dies at 97
His company, the Chiron Corporation, contributed important scientific discoveries toward treatments for H.I.V., hepatitis B, diabetes and more.
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Robert Shapiro, Who Made NutraSweet a Household Name, Dies at 86
His promotion of the sugar substitute was a success. But later, as head of Monsanto, he faced blowback after the company rushed into genetically altered products.
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Pig Kidney Removed From Alabama Woman After Organ Rejection
Towana Looney lived with the kidney longer than any other transplant patient had tolerated an organ from a genetically modified animal.
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For Patients Needing Transplants, Hope Arrives on Tiny Hooves
Some scientists are confident that organs from genetically modified pigs will one day be routinely transplanted into humans. But substantial ethical questions remain.
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The 2023 Good Tech Awards
Toasting a year of breakthroughs (and a few breakdowns) in Silicon Valley and beyond.
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Gene-Sequencing Company Illumina to Sell Cancer Test Developer
The move came two days after a court upheld the Federal Trade Commission’s challenge to the deal on antitrust grounds.
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New Sickle Cell Therapies Will Be Out of Reach Where They Are Needed Most
There is no clear path for African patients to get access to the treatments, which have multimillion-dollar price tags and are highly complex to manufacture and deliver.
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Panel Tells F.D.A. That CRISPR Sickle Cell Cure Is Safe Enough for Patients
The decision by an advisory committee may lead to Food and Drug Administration approval of the first treatment for humans that uses the CRISPR gene-editing system.
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F.D.A. Experts Will Vote on a Cure for Sickle Cell Disease
The treatment from the company Vertex would be the first medicine to use the gene editing tool CRISPR.